Charina M. Ramirez

Mechanisms of autophagy–lysosome dysfunction in neurodegenerative diseases

Diabetes mellitus—Progress and opportunities in the evolving epidemic

Systemic administration of 2‐hydroxypropyl‐β‐cyclodextrin to symptomatic Npc1‐deficient mice slows cholesterol sequestration in the major organs and improves liver function

Cyclodextrin overcomes the transport defect in nearly every organ of NPC1 mice leading to excretion of sequestered cholesterol as bile acid