Citation Impact
Citing Papers
Viral Vectors in Gene Therapy: Where Do We Stand in 2023?
2023
Ocular Hypotensive Effects of an Intratracheally Delivered Liposomal Δ9-Tetrahydrocannabinol Preparation in Rats
2006
Complete Genetic Correction of iPS Cells From Duchenne Muscular Dystrophy
2009 StandoutNobel
Cancer Statistics, 2021
2021 Standout
Screening Libraries to Discover Molecular Design Principles for the Targeted Delivery of mRNA with One-Component Ionizable Amphiphilic Janus Dendrimers Derived from Plant Phenolic Acids
2023 StandoutNobel
Rules for Scoring Respiratory Events in Sleep: Update of the 2007 AASM Manual for the Scoring of Sleep and Associated Events
2012 Standout
The Influence of Genetics on Cystic Fibrosis Phenotypes
2012
Engineering precision nanoparticles for drug delivery
2020 Standout
Circular Intermediates of Recombinant Adeno-Associated Virus Have Defined Structural Characteristics Responsible for Long-Term Episomal Persistence in Muscle Tissue
1998
Genetic Influences on Cystic Fibrosis Lung Disease Severity
2013
Lumacaftor–Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508delCFTR
2015 Standout
New animal models of cystic fibrosis
2011
Interactions Between Secondhand Smoke and Genes That Affect Cystic Fibrosis Lung Disease
2008
Cystic fibrosis
2016 Standout
Cryptic species as a window on diversity and conservation
2006 Standout
Immune responses to gene therapy vectors: influence on vector function and effector mechanisms
2004
Murine models of pulmonary fibrosis
2007
Adeno-associated virus vectors for gene therapy: more pros than cons?
2000
Estimation of the global prevalence and burden of obstructive sleep apnoea: a literature-based analysis
2019 Standout
Ocular Drug Delivery
2010 Standout
Design and development of polymers for gene delivery
2005 Standout
Stimuli-responsive nanocarriers for drug delivery
2013 Standout
Protective Role of Mincle in Bacterial Pneumonia by Regulation of Neutrophil Mediated Phagocytosis and Extracellular Trap Formation
2013
Modifier genes in Mendelian disorders: the example of cystic fibrosis
2010
Recombinant Adeno-Associated Viral Vectors Mediate Long-Term Transgene Expression in Muscle
1997
Interaction between a novel TGFB1 haplotype and CFTR genotype is associated with improved lung function in cystic fibrosis
2008
Amniotic fluid stabilized lipid nanoparticles for in utero intra-amniotic mRNA delivery
2021 StandoutNobel
Complex two-gene modulation of lung disease severity in children with cystic fibrosis
2008
Toxicity of cationic lipids and cationic polymers in gene delivery
2006 Standout
mRNA vaccines for infectious diseases: principles, delivery and clinical translation
2021 StandoutNobel
Gene Therapy and Intracytoplasmatic Sperm Injection (ICSI) – A Review
2008
Genetic medicines: treatment strategies for hereditary disorders
2006
Non-viral vectors for gene-based therapy
2014 Standout
ABGD, Automatic Barcode Gap Discovery for primary species delimitation
2011 Standout
PEGylation as a strategy for improving nanoparticle-based drug and gene delivery
2015 Standout
Priming of hepatitis C virus-specific cytotoxic t lymphocytes in mice following portal vein injection of a liver-specific plasmid DNA
2000 StandoutNobel
In vivo genome editing using Staphylococcus aureus Cas9
2015 StandoutNature
Correlating viral phenotypes with phylogeny: Accounting for phylogenetic uncertainty
2007
Prevalence of sleep-disordered breathing in the general population: the HypnoLaus study
2015 Standout
Precise hit: adeno-associated virus in gene targeting
2005
Scalable Downstream Strategies for Purification of Recombinant Adeno- Associated Virus Vectors in Light of the Properties
2015
The diverse CB1and CB2receptor pharmacology of three plant cannabinoids: Δ9‐tetrahydrocannabinol, cannabidiol and Δ9‐tetrahydrocannabivarin
2007 Standout
Quantification of the Relative Contribution of Environmental and Genetic Factors to Variation in Cystic Fibrosis Lung Function
2010
Mucus-penetrating nanoparticles for drug and gene delivery to mucosal tissues
2008 Standout
Cystic fibrosis genetics: from molecular understanding to clinical application
2014 Standout
Heritability of Respiratory Infection with Pseudomonas aeruginosa in Cystic Fibrosis
2012
Progress and problems with the use of viral vectors for gene therapy
2003 Standout
Adeno-associated virus vector as a platform for gene therapy delivery
2019 Standout
Magnetic Nanoparticles Enhance Adenovirus Transduction In Vitro and In Vivo
2011
The Future of In Utero Gene Therapy
2020
From Virus Evolution to Vector Revolution: Use of Naturally Occurring Serotypes of Adeno-associated Virus (AAV) as Novel Vectors for Human Gene Therapy
2003
Gene delivery systems—gene therapy vectors for cystic fibrosis
2004
Persistence of distinct HIV-1 populations in blood monocytes and naive and memory CD4 T cells during prolonged suppressive HAART
2005
Recombinant adeno-associated virus purification using novel methods improves infectious titer and yield
1999 Standout
Transient Immunosuppression Allows Transgene Expression Following Readministration of Adeno-Associated Viral Vectors
1998
Recombinant Adeno-Associated Virus Gene Therapy for Cystic Fibrosis and α1-Antitrypsin Deficiency
2002
Genetic modifiers of nutritional status in cystic fibrosis
2012
Clinical practice and genetic counseling for cystic fibrosis and CFTR-related disorders
2008
Recombinant AAV Viral Vectors Pseudotyped with Viral Capsids from Serotypes 1, 2, and 5 Display Differential Efficiency and Cell Tropism after Delivery to Different Regions of the Central Nervous System
2004
Bayesian Phylogeography Finds Its Roots
2009 Standout
Microneedles for drug and vaccine delivery
2012 Standout
HIV reservoir size and persistence are driven by T cell survival and homeostatic proliferation
2009 Standout
Genetic Modifiers of Liver Disease in Cystic Fibrosis
2009
Emerging fungal threats to animal, plant and ecosystem health
2012 StandoutNature
0.9% saline is neither normal nor physiological
2016
Unraveling the complex genetic model for cystic fibrosis: pleiotropic effects of modifier genes on early cystic fibrosis-related morbidities
2013
Lung disease modifier genes in cystic fibrosis
2014
Variation in MSRA Modifies Risk of Neonatal Intestinal Obstruction in Cystic Fibrosis
2012
Intravenous Fluids and Acute Kidney Injury
2017 Standout
Recombinant AAV-mediated gene transfer to the retina: gene therapy perspectives
2004
Insights into RNA Virus Mutant Spectrum and Lethal Mutagenesis Events: Replicative Interference and Complementation by Multiple Point Mutants
2007
Early archives of genetically-restricted proviral DNA in the female genital tract after heterosexual transmission of HIV-1
2006
Genes that determine immunology and inflammation modify the basic defect of impaired ion conductance in cystic fibrosis epithelia
2010
Cystic fibrosis
2009
Optogenetics in Neural Systems
2011 Standout
Gene transfer to the lung: Lessons learned from more than 2 decades of CF gene therapy
2008
Barriers to and new approaches for gene therapy and gene delivery in cystic fibrosis
2002
Animal models of acute lung injury
2008 Standout
Long-Term Control of HIV by CCR5 Delta32/Delta32 Stem-Cell Transplantation
2009 Standout
Pathophysiology and Management of Pulmonary Infections in Cystic Fibrosis
2003 Standout
Compacted DNA Nanoparticles Administered to the Nasal Mucosa of Cystic Fibrosis Subjects Are Safe and Demonstrate Partial to Complete Cystic Fibrosis Transmembrane Regulator Reconstitution
2004
A Phase II, Double-Blind, Randomized, Placebo-Controlled Clinical Trial of tgAAVCF Using Maxillary Sinus Delivery in Patients with Cystic Fibrosis with Antrostomies
2002
Prevalence of Neutralizing Antibodies Against Adeno-Associated Virus (AAV) Types 2, 5, and 6 in Cystic Fibrosis and Normal Populations: Implications for Gene Therapy Using AAV Vectors
2006
A Phase I Study of Aerosolized Administration of tgAAVCF to Cystic Fibrosis Subjects with Mild Lung Disease
2001
Repeated Aerosolized AAV-CFTR for Treatment of Cystic Fibrosis: A Randomized Placebo-Controlled Phase 2B Trial
2007
The Unexpected Importance of the Primary Structure of the Hydrophobic Part of One-Component Ionizable Amphiphilic Janus Dendrimers in Targeted mRNA Delivery Activity
2022 StandoutNobel
Optogenetic Dissection of Entorhinal-Hippocampal Functional Connectivity
2013 StandoutScienceNobel
Nanomaterial Delivery Systems for mRNA Vaccines
2021 StandoutNobel
Adeno-Associated Virus Type 5 (AAV5) but Not AAV2 Binds to the Apical Surfaces of Airway Epithelia and Facilitates Gene Transfer
2000
Targeted and Equally Distributed Delivery of mRNA to Organs with Pentaerythritol-Based One-Component Ionizable Amphiphilic Janus Dendrimers
2023 StandoutNobel
One-Component Multifunctional Sequence-Defined Ionizable Amphiphilic Janus Dendrimer Delivery Systems for mRNA
2021 StandoutNobel
Nonviral Vectors for Gene Delivery
2008 Standout
Klebsiella pneumoniae: Going on the Offense with a Strong Defense
2016 Standout
Repeat Transduction in the Mouse Lung by Using Adeno-Associated Virus Vectors with Different Serotypes
2000
A synthesis of two decades of research documenting the effects of noise on wildlife
2015 Standout
Comparative Study of Methods for Detecting Sequence Compartmentalization in Human Immunodeficiency Virus Type 1
2007
CRYPTIC SPECIATION IN THE COSMOPOLITAN AND CLONAL HUMAN PATHOGENIC FUNGUS ASPERGILLUS FUMIGATUS
2005
In Vivo Potency Assay for Adeno-Associated Virus–Based Gene Therapy Vectors Using AAVrh.10 as an Example
2018
Genetic Modifiers Play a Substantial Role in Diabetes Complicating Cystic Fibrosis
2009
Inhaled Nanoformulated mRNA Polyplexes for Protein Production in Lung Epithelium
2019
Animal models of gastrointestinal and liver diseases. Animal models of cystic fibrosis: gastrointestinal, pancreatic, and hepatobiliary disease and pathophysiology
2015
Short- and long-term changes in right whale calling behavior: The potential effects of noise on acoustic communication
2007
Response of Hepatitis C Virus to Long-Term Passage in the Presence of Alpha Interferon: Multiple Mutations and a Common Phenotype
2013 StandoutNobel
Recent advances in DNA taxonomy
2006
CDC Recommendations for Hepatitis C Screening Among Adults — United States, 2020
2020
Increased Replicative Fitness Can Lead to Decreased Drug Sensitivity of Hepatitis C Virus
2014 StandoutNobel
Cystic fibrosis: An update for clinicians. Part 1: Nutrition and gastrointestinal complications
2014
A general species delimitation method with applications to phylogenetic placements
2013 Standout
Genetic Variation and Clinical Heterogeneity in Cystic Fibrosis
2011
Viral Vectors for Gene Therapy
1998
Characterization of Human Antiviral Adaptive Immune Responses during Hepatotropic Virus Infection in HLA-Transgenic Human Immune System Mice
2013 StandoutNobel
Genetic Modifiers of Cystic Fibrosis–Related Diabetes
2013
Integrating mechanisms of pulmonary fibrosis
2011 Standout
Works of Suzanne E. Beck being referenced
Case-control study of hepatitis B and hepatitis C in older adults: Do healthcare exposures contribute to burden of new infections?
2012
Relative Contribution of Genetic and Nongenetic Modifiers to Intestinal Obstruction in Cystic Fibrosis
2006
Heritability of Lung Disease Severity in Cystic Fibrosis
2007
Deposition and Expression of Aerosolized rAAV Vectors in the Lungs of Rhesus Macaques
2002
Effect of low pH on single skeletal muscle myosin mechanics and kinetics
2008
Pediatric Polysomnography
2009
Successful transgene expression with serial doses of aerosolized rAAV2 vectors in rhesus macaques
2003
Phase I Trial of Intranasal and Endobronchial Administration of a Recombinant Adeno-Associated Virus Serotype 2 (rAAV2)-CFTR Vector in Adult Cystic Fibrosis Patients: A Two-Part Clinical Study
2003
Nuclear markers confirm taxonomic status and relationships among highly endangered and closely related right whale species
2005
Repeated Delivery of Adeno-Associated Virus Vectors to the Rabbit Airway
1999
HIV-1 in genital tract and plasma of women: Compartmentalization of viral sequences, coreceptor usage, and glycosylation
2003
Safety of single-dose administration of an adeno-associated virus (AAV)-CFTR vector in the primate lung.
1996