Citation Impact
Citing Papers
The promise and challenge of therapeutic genome editing
2020 StandoutNatureNobel
Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing
2018
Blood–brain barrier breakdown in Alzheimer disease and other neurodegenerative disorders
2018 Standout
Adeno-associated virus vector as a platform for gene therapy delivery
2019 Standout
A balanced view of the cerebrospinal fluid composition and functions: Focus on adult humans
2015
Adeno-Associated Virus-Based Gene Therapy for CNS Diseases
2016
Works of Sofia Hassiotis being referenced
Determination of the role of injection site on the efficacy of intra-CSF enzyme replacement therapy in MPS IIIA mice
2015
A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome
2016
Impact of high-dose, chemically modified sulfamidase on pathology in a murine model of MPS IIIA
2011