Standout Papers
Citation Impact
Citing Papers
rMATS: Robust and flexible detection of differential alternative splicing from replicate RNA-Seq data
2014 Standout
GEPIA2: an enhanced web server for large-scale expression profiling and interactive analysis
2019 Standout
A "Silent" Polymorphism in the MDR 1 Gene Changes Substrate Specificity
2006 StandoutScience
In vivo gene editing in dystrophic mouse muscle and muscle stem cells
2015 Science
The 2016 revision of the World Health Organization classification of lymphoid neoplasms
2016 Standout
Chronic Systemic Therapy With Low-dose Morpholino Oligomers Ameliorates the Pathology and Normalizes Locomotor Behavior in mdx Mice
2010
In Vivo Myogenic Potential of Human CD133+ Muscle-derived Stem Cells: A Quantitative Study
2009
The promise and challenge of therapeutic genome editing
2020 StandoutNatureNobel
Multilineage Cells from Human Adipose Tissue: Implications for Cell-Based Therapies
2001 Standout
A G-to-A transition at the fifth position of intron-32 of the dystrophin gene inactivates a splice-donor site both in vivo and in vitro
2005
Revertant fibres and dystrophin traces in Duchenne muscular dystrophy: Implication for clinical trials
2010
Bone Marrow–Derived Cells Do Not Contribute Significantly to Collagen I Synthesis in a Murine Model of Renal Fibrosis
2006 StandoutNobel
Dystrophin Orchestrates the Epigenetic Profile of Muscle Cells Via miRNAs
2011
Identification of genes in toxicity pathways of trinucleotide-repeat RNA in C. elegans
2014 StandoutNobel
Human Argonaute2 Mediates RNA Cleavage Targeted by miRNAs and siRNAs
2004 Standout
Antisense Masking of an hnRNP A1/A2 Intronic Splicing Silencer Corrects SMN2 Splicing in Transgenic Mice
2008
Nonsense-mediated decay approaches the clinic
2004
Therapeutic targeting of splicing in cancer
2016
MicroRNAs Involved in Molecular Circuitries Relevant for the Duchenne Muscular Dystrophy Pathogenesis Are Controlled by the Dystrophin/nNOS Pathway
2010
Upconverting Nanoparticles
2011 Standout
GRK5 deficiency leads to early Alzheimer-like pathology and working memory impairment
2006
Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle
2003
Metabolic Regulation of Hematopoietic Stem Cells in the Hypoxic Niche
2011 StandoutNobel
The emerging role of lncRNAs in cancer
2015 Standout
Programmable RNA Tracking in Live Cells with CRISPR/Cas9
2016 StandoutNobel
Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy
2006
In-frame Dystrophin Following Exon 51-Skipping Improves Muscle Pathology and Function in the Exon 52–Deficient mdx Mouse
2010
Targeting nuclear RNA for in vivo correction of myotonic dystrophy
2012 Nature
Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy
2011
Muscle stem cells
2002
The dynamics and regulators of cell fate decisions are revealed by pseudotemporal ordering of single cells
2014 Standout
Exon Skipping and Duchenne Muscular Dystrophy Therapy: Selection of the Most Active U1 snRNA Antisense Able to Induce Dystrophin Exon 51 Skipping
2010
Exon skipping and dystrophin restoration in patients with Duchenne muscular dystrophy after systemic phosphorodiamidate morpholino oligomer treatment: an open-label, phase 2, dose-escalation study
2011 Standout
Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy
2009
RNA therapeutics: beyond RNA interference and antisense oligonucleotides
2012 Nobel
Gene Transfer with Microbubble Ultrasound and Plasmid DNA into Skeletal Muscle of Mice: Comparison between Commercially Available Microbubble Contrast Agents
2005
Osteopontin promotes fibrosis in dystrophic mouse muscle by modulating immune cell subsets and intramuscular TGF-β
2009
Efficacy of systemic morpholino exon‐skipping in duchenne dystrophy dogs
2009
Dissecting muscle and neuronal disorders in a Drosophila model of muscular dystrophy
2007 StandoutNobel
Renal fibrosis: an update
2001
A Long Noncoding RNA Controls Muscle Differentiation by Functioning as a Competing Endogenous RNA
2011 Standout
siRNAs: applications in functional genomics and potential as therapeutics
2004
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study
2016 Standout
Long non-coding RNAs: new players in cell differentiation and development
2013 Standout
T-Cell and NK-Cell Posttransplantation Lymphoproliferative Disorders
2007
Human Splicing Finder: an online bioinformatics tool to predict splicing signals
2009 Standout
RNA and Disease
2009
A Cell-Penetrating Scorpion Toxin Enables Mode-Specific Modulation of TRPA1 and Pain
2019 StandoutNobel
Cell-Penetrating Peptides: From Basic Research to Clinics
2017
Long-term persistence of donor nuclei in a Duchenne muscular dystrophy patient receiving bone marrow transplantation
2002
Single hematopoietic stem cells generate skeletal muscle through myeloid intermediates
2003
Insights into RNA Biology from an Atlas of Mammalian mRNA-Binding Proteins
2012 Standout
Tumour-educated macrophages promote tumour progression and metastasis
2004 Standout
Mechanisms of fibrosis: therapeutic translation for fibrotic disease
2012 Standout
The AAV-mediated and RNA-guided CRISPR/Cas9 system for gene therapy of DMD and BMD
2017
Applications of CRISPR technologies in research and beyond
2016 StandoutNobel
Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide
2005
Circ-ZNF609 Is a Circular RNA that Can Be Translated and Functions in Myogenesis
2017 Standout
Microbubble Stability is a Major Determinant of the Efficiency of Ultrasound and Microbubble Mediated in vivo Gene Transfer
2009 StandoutNobel
Molecular mechanisms of muscular dystrophies: old and new players
2006
Enhancement of SMN2 Exon 7 Inclusion by Antisense Oligonucleotides Targeting the Exon
2007
Highly Efficient, Functional Engraftment of Skeletal Muscle Stem Cells in Dystrophic Muscles
2008
Alternative Splicing: Therapeutic Target and Tool
2006
Dystrophin levels as low as 30% are sufficient to avoid muscular dystrophy in the human
2007
Micelles and nanoparticles for ultrasonic drug and gene delivery
2008
Biomarkers for epithelial-mesenchymal transitions
2009 Standout
CRISPR-Based Technologies for the Manipulation of Eukaryotic Genomes
2016 Standout
Gold Nanoparticles for Biology and Medicine
2010 Standout
Cornerstones of CRISPR–Cas in drug discovery and therapy
2016 StandoutNobel
Delivery of siRNA to the mouse brain by systemic injection of targeted exosomes
2011 Standout
Col1a2 enhancer regulates collagen activity during development and in adult tissue repair
2004
A Putative Src Homology 3 Domain Binding Motif but Not the C-terminal Dystrophin WW Domain Binding Motif Is Required for Dystroglycan Function in Cellular Polarity in Drosophila
2007 StandoutNobel
Intracellular amyloid-β in Alzheimer's disease
2007 Standout
Galectin expression in cancer diagnosis and prognosis: A systematic review
2015
Efficient genome editing in the mouse brain by local delivery of engineered Cas9 ribonucleoprotein complexes
2017 StandoutNobel
Peroxynitrite: biochemistry, pathophysiology and development of therapeutics
2007 Standout
Multifunctional polymeric micelles for delivery of drugs and siRNA
2014
Local Dystrophin Restoration with Antisense Oligonucleotide PRO051
2007
Long Noncoding RNAs: Cellular Address Codes in Development and Disease
2013 Standout
Glycosylation in cancer: mechanisms and clinical implications
2015 Standout
Hepatic Stellate Cells: Protean, Multifunctional, and Enigmatic Cells of the Liver
2008 Standout
Allogeneic mesoangioblasts give rise to alpha-sarcoglycan expressing fibers when transplanted into dystrophic mice
2006
Gene regulation by long non-coding RNAs and its biological functions
2020 Standout
Small RNAs are modified with N-glycans and displayed on the surface of living cells
2021 StandoutNobel
Exon 45 Skipping Through U1-snRNA Antisense Molecules Recovers the Dys-nNOS Pathway and Muscle Differentiation in Human DMD Myoblasts
2012
Safety Pharmacology and Genotoxicity Evaluation of AVI-4658
2010
Comparative Analysis of Antisense Oligonucleotide Sequences for Targeted Skipping of Exon 51 During Dystrophin Pre-mRNA Splicing in Human Muscle
2007
Mechanical force prolongs acute inflammation via T‐cell‐dependent pathways during scar formation
2011
Relationship between Schistosomiasis and Bladder Cancer
1999
The Next Generation of Platinum Drugs: Targeted Pt(II) Agents, Nanoparticle Delivery, and Pt(IV) Prodrugs
2016 Standout
Antisense Oligonucleotides: An Emerging Area in Drug Discovery and Development
2020
RNA Targeting Therapeutics: Molecular Mechanisms of Antisense Oligonucleotides as a Therapeutic Platform
2010
Long-term persistence of donor nuclei in a Duchenne muscular dystrophy patient receiving bone marrow transplantation
2002
Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model
2006
How mitochondria produce reactive oxygen species
2008 Standout
Degradable Controlled-Release Polymers and Polymeric Nanoparticles: Mechanisms of Controlling Drug Release
2016 Standout
Muscle-specific expression of insulin-like growth factor I counters muscle decline in mdx mice
2002
A Side Order of Stem Cells: The SP Phenotype
2006
Function and Genetics of Dystrophin and Dystrophin-Related Proteins in Muscle
2002
miR‐31 modulates dystrophin expression: new implications for Duchenne muscular dystrophy therapy
2011
Wound Healing: A Cellular Perspective
2018 Standout
A Near-IR Reversible Fluorescent Probe Modulated by Selenium for Monitoring Peroxynitrite and Imaging in Living Cells
2011 Standout
Satellite Cells and the Muscle Stem Cell Niche
2013 Standout
Splicing of a Critical Exon of Human Survival Motor Neuron Is Regulated by a Unique Silencer Element Located in the Last Intron
2006
Cellular and Molecular Regulation of Muscle Regeneration
2004 Standout
Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy
2017
Myogenic Potential of Muscle Side and Main Population Cells after Intravenous Injection into Sub-lethally Irradiated mdx Mice
2005
Generation of skeletal muscle stem/progenitor cells from murine induced pluripotent stem cells
2010 StandoutNobel
A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice
2009
The glucuronyltransferase B4GAT1 is required for initiation of LARGE-mediated α-dystroglycan functional glycosylation
2014
Works of Qi Long Lu being referenced
Elusive sources of variability of dystrophin rescue by exon skipping
2015
Posttransplant cutaneous lymphoma
1993
Expression of bcl‐2 and p53 oncoproteins in schistosomiasis‐associated transitional and squamous cell carcinoma of urinary bladder
1997
Octa-guanidine Morpholino Restores Dystrophin Expression in Cardiac and Skeletal Muscles and Ameliorates Pathology in Dystrophic mdx Mice
2009
Absence of Post-phosphoryl Modification in Dystroglycanopathy Mouse Models and Wild-type Tissues Expressing Non-laminin Binding Form of α-Dystroglycan
2012
Dose-dependent restoration of dystrophin expression in cardiac muscle of dystrophic mice by systemically delivered morpholino
2009
Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology
2006 StandoutNobel
Pluronic block copolymers: Novel functions in ultrasound-mediated gene transfer and against cell damage
2005
One-year Treatment of Morpholino Antisense Oligomer Improves Skeletal and Cardiac Muscle Functions in Dystrophic mdx Mice
2010
Peptide‐Morpholino Conjugate: A Promising Therapeutic for Duchenne Muscular Dystrophy
2009
T-Cell-Dependent Fibrosis in the mdx Dystrophic Mouse
2000
Relocalization of neuronal nitric oxide synthase (nNOS) as a marker for complete restoration of the dystrophin associated protein complex in skeletal muscle
2002
Long-Term Rescue of Dystrophin Expression and Improvement in Muscle Pathology and Function in Dystrophic mdx Mice by Peptide-Conjugated Morpholino
2012
High expressions of galectin-1 and VEGF are associated with poor prognosis in gastric cancer patients
2013
A New Blocking Method for Application of Murine Monoclonal Antibody to Mouse Tissue Sections
1998
Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse
2003
Adenovirus-Based Targeting in Myoblasts Is Hampered by Nonhomologous Vector Integration
2008
Massive Idiosyncratic Exon Skipping Corrects the Nonsense Mutation in Dystrophic Mouse Muscle and Produces Functional Revertant Fibers by Clonal Expansion
2000
Na+,K+-ATPase activity is inhibited in cultured intestinal epithelial cells by endotoxin or nitric oxide
2005
Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles
2004 StandoutNobel
Effective rescue of dystrophin improves cardiac function in dystrophin-deficient mice by a modified morpholino oligomer
2008