Citation Impact
Citing Papers
Generation of Pluripotent Stem Cells from Adult Mouse Liver and Stomach Cells
2008 StandoutScienceNobel
SuFEx-enabled, agnostic discovery of covalent inhibitors of human neutrophil elastase
2019 StandoutNobel
RNA-Guided Human Genome Engineering via Cas9
2013 StandoutScience
Cancer Regression in Patients After Transfer of Genetically Engineered Lymphocytes
2006 StandoutScience
Tumor imaging by means of proteolytic activation of cell-penetrating peptides
2004 StandoutNobel
Diversity oriented clicking delivers β-substituted alkenyl sulfonyl fluorides as covalent human neutrophil elastase inhibitors
2022 StandoutNobel
The promise and challenge of therapeutic genome editing
2020 StandoutNatureNobel
Engineering precision nanoparticles for drug delivery
2020 Standout
Implications of the Human Genome Project for Medical Science
2001
Short-Term Effects of Nose-Only Cigarette Smoke Exposure on Glutathione Redox Homeostasis, Cytochrome P450 1A1/2 and Respiratory Enzyme Activities in Mice Tissues
2013 Standout
Stem cells, cancer, and cancer stem cells
2001 StandoutNature
The Body-Mass Index, Airflow Obstruction, Dyspnea, and Exercise Capacity Index in Chronic Obstructive Pulmonary Disease
2004 Standout
T-cell-receptor gene therapy
2002
Osteoblastic cells regulate the haematopoietic stem cell niche
2003 StandoutNature
Human Primary Immunodeficiency Diseases
2007
State-of-the-art gene-based therapies: the road ahead
2011
Design and development of polymers for gene delivery
2005 Standout
Genotoxicity of Retroviral Integration In Hematopoietic Cells
2006
Incorporation of pseudouridine into mRNA enhances translation by diminishing PKR activation
2010 StandoutNobel
Upping the Ante: Recent Advances in Direct Reprogramming
2009
Current perceptions of cardiovascular gene therapy
2003
Comprehensive computational design of mCreI homing endonuclease cleavage specificity for genome engineering
2011 StandoutNobel
A congenital mutation of the novel gene LRRC8 causes agammaglobulinemia in humans
2003
Mediators of Chronic Obstructive Pulmonary Disease
2004
Gene therapy clinical trials worldwide to 2007—an update
2007
Molecular Imaging
2001
In vivo genome editing using Staphylococcus aureus Cas9
2015 StandoutNature
In Vivo Selection for Human and Murine Hematopoietic Cells Transduced with a Therapeutic MGMT Lentiviral Vector that Inhibits HIV Replication
2004
Stem cell route to neuromuscular therapies
2002
Viruses and tumours – an update
2004
Gene Therapy
2001
Computational redesign of endonuclease DNA binding and cleavage specificity
2006 StandoutNatureNobel
Development and Applications of CRISPR-Cas9 for Genome Engineering
2014 Standout
Progress and problems with the use of viral vectors for gene therapy
2003 Standout
SWELL1, a Plasma Membrane Protein, Is an Essential Component of Volume-Regulated Anion Channel
2014 StandoutNobel
Efficacy of Gene Therapy for X-Linked Severe Combined Immunodeficiency
2010
Exosomes facilitate therapeutic targeting of oncogenic KRAS in pancreatic cancer
2017 StandoutNature
Hsp70 and CHIP Selectively Mediate Ubiquitination and Degradation of Hypoxia-inducible Factor (HIF)-1α but Not HIF-2α
2009 StandoutNobel
Revealing the world of RNA interference
2004 StandoutNatureNobel
The effects of SCF/G-CSF prestimulation on radiation sensitivity and engraftment in nonmyeloablated murine hosts
2001
Highly efficient endogenous human gene correction using designed zinc-finger nucleases
2005 Nature
Repertoires of Autophagy in the Pathogenesis of Ocular Diseases
2015 Standout
Gene therapy: trials and tribulations
2000
Meganucleases and Other Tools for Targeted Genome Engineering: Perspectives and Challenges for Gene Therapy
2011
Gene therapy for optic nerve disease
2004
Gene therapy clinical trials worldwide 1989–2004—an overview
2004
Mesenchymal stem cells within tumour stroma promote breast cancer metastasis
2007 StandoutNature
Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics
2001
Chronic obstructive pulmonary disease: molecular and cellularmechanisms
2003
The cancer genome
2009 StandoutNature
Repurposing CRISPR as an RNA-Guided Platform for Sequence-Specific Control of Gene Expression
2013 StandoutNobel
Genome-editing Technologies for Gene and Cell Therapy
2016
Global Strategy for the Diagnosis, Management, and Prevention of Chronic Obstructive Pulmonary Disease
2012 Standout
Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?
2016
Genome Editing B.C. (Before CRISPR): Lasting Lessons from the “Old Testament”
2018
Anti-Human Immunodeficiency Virus Hematopoietic Progenitor Cell-Delivered Ribozyme in a Phase I Study: Myeloid and Lymphoid Reconstitution in Human Immunodeficiency Virus Type-1–Infected Patients
2004
Cationic liposomes for gene delivery
2005
The Unexpected Importance of the Primary Structure of the Hydrophobic Part of One-Component Ionizable Amphiphilic Janus Dendrimers in Targeted mRNA Delivery Activity
2022 StandoutNobel
T Cell Homeostasis
2001
High Efficiency TCR Gene Transfer into Primary Human Lymphocytes Affords Avid Recognition of Melanoma Tumor Antigen Glycoprotein 100 and Does Not Alter the Recognition of Autologous Melanoma Antigens
2003
Inhibiting HIV-1 infection in human T cells by lentiviral-mediated delivery of small interfering RNA against CCR5
2002 Nobel
A tragic setback
2002 Nature
Isolating gene-corrected stem cells without drug selection
2005 StandoutNobel
In vivo selection of genetically modified erythroblastic progenitors leads to long-term correction of β-thalassemia
2008
Correction of ADA-SCID by Stem Cell Gene Therapy Combined with Nonmyeloablative Conditioning
2002 Science
Lifetime correction of genetic deficiency in mice with a single injection of helper-dependent adenoviral vector
2001
Generation of Mouse Induced Pluripotent Stem Cells Without Viral Vectors
2008 StandoutScienceNobel
Targeting transgene expression to antigen-presenting cells derived from lentivirus-transduced engrafting human hematopoietic stem/progenitor cells
2002
One-Component Multifunctional Sequence-Defined Ionizable Amphiphilic Janus Dendrimer Delivery Systems for mRNA
2021 StandoutNobel
Genetically increased angiotensin I-converting enzyme level and renal complications in the diabetic mouse
2001 StandoutNobel
Nonviral Vectors for Gene Delivery
2008 Standout
A pH-Sensitive Polymer That Enhances Cationic Lipid-Mediated Gene Transfer
2001
Modeling hepatitis C virus infection using human induced pluripotent stem cells
2012 StandoutNobel
Generating the optimal mRNA for therapy: HPLC purification eliminates immune activation and improves translation of nucleoside-modified, protein-encoding mRNA
2011 StandoutNobel
Reprogramming homing endonuclease specificity through computational design and directed evolution
2013 StandoutNobel
[Progress in gene therapy].
2011
Reversible Photocontrol of Biological Systems by the Incorporation of Molecular Photoswitches
2013 StandoutNobel
Unsaturated Cationic Ortho Esters for Endosome Permeation in Gene Delivery
2007
megaTALs: a rare-cleaving nuclease architecture for therapeutic genome engineering
2013 StandoutNobel
Delivery technologies for genome editing
2017
The Notch Ligand Jagged-1 Represents a Novel Growth Factor of Human Hematopoietic Stem Cells
2000
Viral Vectors for Gene Therapy: Translational and Clinical Outlook
2015
Multiple Applications For Replication‐Defective Herpes Simplex Virus Vectors
2001
Targeted Delivery of mRNA with One-Component Ionizable Amphiphilic Janus Dendrimers
2021 StandoutNobel
Cas9 interrogates DNA in discrete steps modulated by mismatches and supercoiling
2020 StandoutNobel
The Role of Serine Proteases and Antiproteases in the Cystic Fibrosis Lung
2015
In vivo hematopoietic stem cell modification by mRNA delivery
2023 StandoutScienceNobel
Targeted gene knock-in by homology-directed genome editing using Cas9 ribonucleoprotein and AAV donor delivery
2017 StandoutNobel
Polysialic acid governs T-cell development by regulating progenitor access to the thymus
2009 StandoutNobel
CRISPR-Cas guides the future of genetic engineering
2018 StandoutScienceNobel
The Discovery of Zinc Fingers and Their Applications in Gene Regulation and Genome Manipulation
2010 Nobel
Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles
2004 StandoutNobel
Innate or Adaptive Immunity? The Example of Natural Killer Cells
2011 StandoutScience
Gene Therapy
2019
Nontoxic nanopore electroporation for effective intracellular delivery of biological macromolecules
2019 StandoutNobel
Works of Patrick Nusbaum being referenced
Proteinase 3, a Potent Secretagogue in Airways, Is Present in Cystic Fibrosis Sputum
1999
Optimization of Retroviral Gene Transfer Protocol to Maintain the Lymphoid Potential of Progenitor Cells
2001
Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease
2000 StandoutScience