Nicolas Wein

In vivo human T cell engineering with enveloped delivery vehicles

Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders

Efficient Skipping of Single Exon Duplications in DMD Patient-Derived Cell Lines Using an Antisense Oligonucleotide Approach

Efficient bypass of mutations in dysferlin deficient patient cells by antisense-induced exon skipping