Citation Impact
Citing Papers
rMATS: Robust and flexible detection of differential alternative splicing from replicate RNA-Seq data
2014 Standout
A conformational checkpoint between DNA binding and cleavage by CRISPR-Cas9
2017 StandoutNobel
Genetic Reactivation of Cone Photoreceptors Restores Visual Responses in Retinitis Pigmentosa
2010 Science
From oxygen to erythropoietin: Relevance of hypoxia for retinal development, health and disease
2011
Complete Genetic Correction of iPS Cells From Duchenne Muscular Dystrophy
2009 StandoutNobel
Superior In vivo Transduction of Human Hepatocytes Using Engineered AAV3 Capsid
2016 StandoutNobel
Regulation of microRNA function in animals
2018 Standout
Cpf1 Is a Single RNA-Guided Endonuclease of a Class 2 CRISPR-Cas System
2015 Standout
Parvovirus glycan interactions
2014
Circular RNAs are a large class of animal RNAs with regulatory potency
2013 StandoutNature
Optogenetics
2010 Standout
AAV Capsid Structure and Cell Interactions
2011
Restoration of Human Dystrophin Following Transplantation of Exon-Skipping-Engineered DMD Patient Stem Cells into Dystrophic Mice
2007
Modular regulatory principles of large non-coding RNAs
2012 StandoutNature
Age-Related Macular Degeneration
2008 Standout
Regulation of microRNA biogenesis
2014 Standout
MicroRNAs Involved in Molecular Circuitries Relevant for the Duchenne Muscular Dystrophy Pathogenesis Are Controlled by the Dystrophin/nNOS Pathway
2010
Intracellular transport of recombinant adeno-associated virus vectors
2012
Efficient mutagenesis of the rhodopsin gene in rod photoreceptor neurons in mice
2011
The emerging role of lncRNAs in cancer
2015 Standout
Targeting RNA splicing for disease therapy
2013
Optogenetics: 10 years of microbial opsins in neuroscience
2015 Standout
Ageing as a risk factor for neurodegenerative disease
2019 Standout
FUS stimulates microRNA biogenesis by facilitating co‐transcriptional Drosha recruitment
2012
The role of DNA base excision repair in brain homeostasis and disease
2015
The dynamics and regulators of cell fate decisions are revealed by pseudotemporal ordering of single cells
2014 Standout
Exon Skipping and Duchenne Muscular Dystrophy Therapy: Selection of the Most Active U1 snRNA Antisense Able to Induce Dystrophin Exon 51 Skipping
2010
The multilayered complexity of ceRNA crosstalk and competition
2014 StandoutNature
Age-related macular degeneration
2012 Standout
A Long Noncoding RNA Controls Muscle Differentiation by Functioning as a Competing Endogenous RNA
2011 Standout
Metazoan MicroRNAs
2018 Standout
Reactive oxygen species (ROS) as pleiotropic physiological signalling agents
2020 Standout
Long non-coding RNAs: new players in cell differentiation and development
2013 Standout
Natural RNA circles function as efficient microRNA sponges
2013 StandoutNature
Germline viral “fossils” guide in silico reconstruction of a mid-Cenozoic era marsupial adeno-associated virus
2016
The widespread regulation of microRNA biogenesis, function and decay
2010 Standout
Characterizing Light-Regulated Retinal MicroRNAs Reveals Rapid Turnover as a Common Property of Neuronal MicroRNAs
2010
Viral-mediated gene therapy for the muscular dystrophies: Successes, limitations and recent advances
2006
RNA and Disease
2009
MicroRNA biogenesis pathways in cancer
2015 Standout
Gene therapy for hemophilia
2015
Ultra light-sensitive and fast neuronal activation with the Ca2+-permeable channelrhodopsin CatCh
2011
Mitochondria in the signaling pathways that control longevity and health span
2019
The potential of adeno-associated viral vectors for gene delivery to muscle tissue
2014
Cystic fibrosis genetics: from molecular understanding to clinical application
2014 Standout
In Silico Reconstruction of the Viral Evolutionary Lineage Yields a Potent Gene Therapy Vector
2015
Conformational control of DNA target cleavage by CRISPR–Cas9
2015 StandoutNatureNobel
The long noncoding RNA Vax2os1 controls the cell cycle progression of photoreceptor progenitors in the mouse retina
2011
Insights into RNA Biology from an Atlas of Mammalian mRNA-Binding Proteins
2012 Standout
Novel Lipofuscin Bisretinoids Prominent in Human Retina and in a Model of Recessive Stargardt Disease
2009
Restoring the ON Switch in Blind Retinas: Opto-mGluR6, a Next-Generation, Cell-Tailored Optogenetic Tool
2015
Taking Stock of Retinal Gene Therapy: Looking Back and Moving Forward
2017
Adeno-associated virus vector as a platform for gene therapy delivery
2019 Standout
Applications of CRISPR technologies in research and beyond
2016 StandoutNobel
Circ-ZNF609 Is a Circular RNA that Can Be Translated and Functions in Myogenesis
2017 Standout
Biology and Applications of CRISPR Systems: Harnessing Nature’s Toolbox for Genome Engineering
2016 StandoutNobel
Molecular mechanisms of muscular dystrophies: old and new players
2006
Novel Adeno-associated Viruses Derived From Pig Tissues Transduce Most Major Organs in Mice
2014
Effect of Genome Size on AAV Vector Packaging
2009
CRISPR-Based Technologies for the Manipulation of Eukaryotic Genomes
2016 Standout
Cornerstones of CRISPR–Cas in drug discovery and therapy
2016 StandoutNobel
Endogenous microRNA sponges: evidence and controversy
2016 Standout
A Putative Src Homology 3 Domain Binding Motif but Not the C-terminal Dystrophin WW Domain Binding Motif Is Required for Dystroglycan Function in Cellular Polarity in Drosophila
2007 StandoutNobel
Characterization of Genome Integrity for Oversized Recombinant AAV Vector
2009
VEGF in Signaling and Disease: Beyond Discovery and Development
2019 Standout
Optogenetics in Neural Systems
2011 Standout
Gene regulation by long non-coding RNAs and its biological functions
2020 Standout
The Oscillating miRNA 959-964 Cluster Impacts Drosophila Feeding Time and Other Circadian Outputs
2012 StandoutNobel
starBase v2.0: decoding miRNA-ceRNA, miRNA-ncRNA and protein–RNA interaction networks from large-scale CLIP-Seq data
2013 Standout
In Vivo CRISPR/Cas9 Gene Editing Corrects Retinal Dystrophy in the S334ter-3 Rat Model of Autosomal Dominant Retinitis Pigmentosa
2015
Exon 45 Skipping Through U1-snRNA Antisense Molecules Recovers the Dys-nNOS Pathway and Muscle Differentiation in Human DMD Myoblasts
2012
Delivery and Specificity of CRISPR/Cas9 Genome Editing Technologies for Human Gene Therapy
2015
Adenoviral Vector-Delivered Pigment Epithelium-Derived Factor for Neovascular Age-Related Macular Degeneration: Results of a Phase I Clinical Trial
2006
The Future Looks Brighter After 25 Years of Retinal Gene Therapy
2017
Advances in Gene Therapy for Diseases of the Eye
2016
The Development and Application of Optogenetics
2011 Standout
Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes.
2017
RNA Interference–Mediated Suppression and Replacement of Human Rhodopsin In Vivo
2007
Fluorescence Lifetime Measurements and Biological Imaging
2010 Standout
CRISPR-Cas: biology, mechanisms and relevance
2016 StandoutNobel
mir-276a strengthens Drosophila circadian rhythms by regulating timeless expression
2016 StandoutNobel
Mammalian Sirtuins: Biological Insights and Disease Relevance
2010 Standout
miR‐31 modulates dystrophin expression: new implications for Duchenne muscular dystrophy therapy
2011
Long Noncoding RNAs: Past, Present, and Future
2013 Standout
AAV.Dysferlin Overlap Vectors Restore Function in Dysferlinopathy Animal Models
2015
Satellite Cells and the Muscle Stem Cell Niche
2013 Standout
Severe Retinal Degeneration Caused by a Novel Rhodopsin Mutation
2010 StandoutNobel
SIRT1 Activation Confers Neuroprotection in Experimental Optic Neuritis
2007
Works of Mariacarmela Allocca being referenced
Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice
2008
Preferential silencing of a common dominant rhodopsin mutation does not inhibit retinal degeneration in a transgenic model
2006
Isolation and evaluation of novel adeno-associated virus sequences from porcine tissues
2009
AAV-mediated gene transfer for retinal diseases
2006
Systemic but not intraocular Epo Gene Transfer Protects the Retina from Light-and Genetic-Induced Degeneration
2004
Chimeric Adeno-Associated Virus/Antisense U1 Small Nuclear RNA Effectively Rescues Dystrophin Synthesis and Muscle Function by Local Treatment of mdx Mice
2006
Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model
2006
AAV-Mediated Gene Replacement, Either Alone or in Combination with Physical and Pharmacological Agents, Results in Partial and Transient Protection from Photoreceptor Degeneration Associated with βPDE Deficiency
2011
Novel Adeno-Associated Virus Serotypes Efficiently Transduce Murine Photoreceptors
2007
Aag-initiated base excision repair promotes ischemia reperfusion injury in liver, brain, and kidney
2014