Citation Impact
Citing Papers
Comprehensive computational design of ordered peptide macrocycles
2017 StandoutScienceNobel
In Vitro and In Vivo Gene Therapy Vector Evolution via Multispecies Interbreeding and Retargeting of Adeno-Associated Viruses
2008
Super-resolution imaging of nuclear import of adeno-associated virus in live cells
2015
Oligonucleotide conjugated multi-functional adeno-associated viruses
2018
Telomerase gene therapy in adult and old mice delays aging and increases longevity without increasing cancer
2012
The promise and challenge of therapeutic genome editing
2020 StandoutNatureNobel
CD8+ T Cell Recognition of Epitopes Within the Capsid of Adeno-associated Virus 8–based Gene Transfer Vectors Depends on Vectors’ Genome
2013
Engineering adeno-associated viruses for clinical gene therapy
2014
Superior In vivo Transduction of Human Hepatocytes Using Engineered AAV3 Capsid
2016 StandoutNobel
AAV9-mediated telomerase activation does not accelerate tumorigenesis in the context of oncogenic K-Ras-induced lung cancer
2018
In vivo genetic engineering of murine pancreatic beta cells mediated by single-stranded adeno-associated viral vectors of serotypes 6, 8 and 9
2011
AAV Capsid Structure and Cell Interactions
2011
Selection and evaluation of clinically relevant AAV variants in a xenograft liver model
2013 Nature
Gene therapy for neurological disorders: progress and prospects
2018
Off-target-free gene delivery by affinity-purified receptor-targeted viral vectors
2015
Adeno-Associated Virus Gene Therapy: Translational Progress and Future Prospects in the Treatment of Heart Failure
2018
Tropism-modified AAV Vectors Overcome Barriers to Successful Cutaneous Therapy
2014
Adeno-associated virus (AAV) capsid genes isolated from rat and mouse liver genomic DNA define two new AAV species distantly related to AAV-5
2006
Applications of genome editing technology in the targeted therapy of human diseases: mechanisms, advances and prospects
2020 Standout
Hallmarks of aging: An expanding universe
2023 Standout
Applications of CRISPR-Cas Enzymes in Cancer Therapeutics and Detection
2018 StandoutNobel
PLGA-based nanoparticles: An overview of biomedical applications
2012 Standout
Altering AAV tropism with mosaic viral capsids
2005
Ocular Drug Delivery
2010 Standout
Viral vectors: from virology to transgene expression
2008
Particle invasion, survival, and non-ergodicity in 2D diffusion processes with space-dependent diffusivity
2014
Viruses as Building Blocks for Materials and Devices
2007
Selective Loss of Brain-Derived Neurotrophic Factor in the Dentate Gyrus Attenuates Antidepressant Efficacy
2007
VAMP-associated protein-A and oxysterol-binding protein–related protein 3 promote the entry of late endosomes into the nucleoplasmic reticulum
2018
Virus-mediated gene delivery for human gene therapy
2012
Locating proteins in the cell using TargetP, SignalP and related tools
2007 Standout
Toxicity of cationic lipids and cationic polymers in gene delivery
2006 Standout
In situ immune response and mechanisms of cell damage in central nervous system of fatal cases microcephaly by Zika virus
2018 Standout
Generation of Novel AAV Variants by Directed Evolution for Improved CFTR Delivery to Human Ciliated Airway Epithelium
2009
Biological roles of glycans
2016 Standout
Cellular senescence in ageing: from mechanisms to therapeutic opportunities
2020 Standout
Evolution of a designed protein assembly encapsulating its own RNA genome
2017 StandoutNatureNobel
NMDA receptor blockade at rest triggers rapid behavioural antidepressant responses
2011 StandoutNature
Preferential labeling of inhibitory and excitatory cortical neurons by endogenous tropism of adeno-associated virus and lentivirus vectors
2009
Non-viral vectors for gene-based therapy
2014 Standout
Comprehensive computational design of mCreI homing endonuclease cleavage specificity for genome engineering
2011 StandoutNobel
PEGylation as a strategy for improving nanoparticle-based drug and gene delivery
2015 Standout
Heparan sulfate proteoglycan as a cell-surface endocytosis receptor
2013
Human Immune Responses to Adeno-Associated Virus (AAV) Vectors
2020
Parkinson's disease
2015 Standout
AAV Hybrid Serotypes: Improved Vectors for Gene Delivery
2005
Microfluidic device for stem cell differentiation and localized electroporation of postmitotic neurons
2014
Parkinson's Disease: Gene Therapies
2012
Distinct Neuronal Coding Schemes in Memory Revealed by Selective Erasure of Fast Synchronous Synaptic Transmission
2012 StandoutNobel
AAV-8 and AAV-9 Vectors Cooperate with Serum Proteins Differently Than AAV-1 and AAV-6
2018
Directed evolution of adeno-associated virus yields enhanced gene delivery vectors
2006
Capsid antigen presentation flags human hepatocytes for destruction after transduction by adeno-associated viral vectors
2009
Virus entry: molecular mechanisms and biomedical applications
2004
Cellular uptake of extracellular vesicles is mediated by clathrin-independent endocytosis and macropinocytosis
2017
Adeno-associated virus (AAV) vectors in cancer gene therapy
2016
The potential of adeno-associated viral vectors for gene delivery to muscle tissue
2014
Gene Transfer Properties and Structural Modeling of Human Stem Cell-derived AAV
2014
The AAV Vector Toolkit: Poised at the Clinical Crossroads
2012
In Silico Reconstruction of the Viral Evolutionary Lineage Yields a Potent Gene Therapy Vector
2015
Adeno-associated virus vector as a platform for gene therapy delivery
2019 Standout
Inner Limiting Membrane Barriers to AAV-mediated Retinal Transduction From the Vitreous
2009
Gene delivery systems—gene therapy vectors for cystic fibrosis
2004
A directed evolution approach to select for novel Adeno-associated virus capsids on an HIV-1 producer T cell line
2017
Genome-Scale Identification of SARS-CoV-2 and Pan-coronavirus Host Factor Networks
2020 StandoutNobel
Adeno-associated viral vectors for the treatment of hemophilia
2015
Novel Adeno-associated Viruses Derived From Pig Tissues Transduce Most Major Organs in Mice
2014
The HCV Life Cycle: In vitro Tissue Culture Systems and Therapeutic Targets
2014 Standout
Comparative Study of Liver Gene Transfer With AAV Vectors Based on Natural and Engineered AAV Capsids
2015
AAV Vectors Vaccines Against Infectious Diseases
2014
The Hallmarks of Aging
2013 Standout
Specificities of secretion and uptake of exosomes and other extracellular vesicles for cell-to-cell communication
2018 Standout
Establishing chitosan coated PLGA nanosphere platform loaded with wide variety of nucleic acid by complexation with cationic compound for gene delivery
2007
Mechanisms of Receptor‐Mediated Nuclear Import and Nuclear Export
2005
Molecular signatures of disease brain endothelia provide new sites for CNS-directed enzyme therapy
2009
A Superhighway to Virus Infection
2006
PEG conjugation moderately protects adeno‐associated viral vectors against antibody neutralization
2005
Optogenetics in Neural Systems
2011 Standout
Adeno-Associated Virus Vectors for Short Hairpin RNA Expression
2005
Functional Roles of the IgM Fc Receptor in the Immune System
2019 StandoutNobel
Development of Virus-Like Particle Technology from Small Highly Symmetric to Large Complex Virus-Like Particle Structures
2013 Standout
Safe and Effective In Vivo Targeting and Gene Editing in Hematopoietic Stem Cells: Strategies for Accelerating Development
2021 StandoutNobel
S/MAR Element Facilitates Episomal Long-Term Persistence of Adeno-Associated Virus Vector Genomes in Proliferating Cells
2017
Scalable Recombinant Adeno-Associated Virus Production Using Recombinant Herpes Simplex Virus Type 1 Coinfection of Suspension-Adapted Mammalian Cells
2009
Overexpression of TOSO in CLL is triggered by B-cell receptor signaling and associated with progressive disease
2008
Self-Assembly of “S-Bilayers”, a Step Toward Expanding the Dimensionality of S-Layer Assemblies
2013 StandoutNobel
The Unexpected Importance of the Primary Structure of the Hydrophobic Part of One-Component Ionizable Amphiphilic Janus Dendrimers in Targeted mRNA Delivery Activity
2022 StandoutNobel
Optogenetic Dissection of Entorhinal-Hippocampal Functional Connectivity
2013 StandoutScienceNobel
Ionizable Lipid Nanoparticles for In Vivo mRNA Delivery to the Placenta during Pregnancy
2023 StandoutNobel
Erratum: Gene therapy for neurological disorders: progress and prospects
2018
In Vivo–Directed Evolution of a New Adeno-Associated Virus for Therapeutic Outer Retinal Gene Delivery from the Vitreous
2013
Structure of a designed tetrahedral protein assembly variant engineered to have improved soluble expression
2015 StandoutNobel
Targeted and Equally Distributed Delivery of mRNA to Organs with Pentaerythritol-Based One-Component Ionizable Amphiphilic Janus Dendrimers
2023 StandoutNobel
Quantifying the Dynamics of Protein Self-Organization Using Deep Learning Analysis of Atomic Force Microscopy Data
2020 StandoutNobel
Adeno-Associated Virus Type 2 VP2 Capsid Protein Is Nonessential and Can Tolerate Large Peptide Insertions at Its N Terminus
2004
One-Component Multifunctional Sequence-Defined Ionizable Amphiphilic Janus Dendrimer Delivery Systems for mRNA
2021 StandoutNobel
Efficient and stable transduction of resting B lymphocytes and primary chronic lymphocyte leukemia cells using measles virus gp displaying lentiviral vectors
2009
Cryo-electron Microscopy Reconstruction and Stability Studies of the Wild Type and the R432A Variant of Adeno-associated Virus Type 2 Reveal that Capsid Structural Stability Is a Major Factor in Genome Packaging
2016
Capsid Antibodies to Different Adeno-Associated Virus Serotypes Bind Common Regions
2013
Ion-dependent protein–surface interactions from intrinsic solvent response
2021 StandoutNobel
Self-Assembling 2D Arrays with de Novo Protein Building Blocks
2019 StandoutNobel
Ionizable lipid nanoparticles deliver mRNA to pancreatic β cells via macrophage-mediated gene transfer
2023 StandoutNobel
Adeno-Associated Virus Structural Biology as a Tool in Vector Development
2013
PEGylated Viral Nanoparticles for Biomedicine: The Impact of PEG Chain Length on VNP Cell Interactions In Vitro and Ex Vivo
2009
Crystal Engineering of Self-Assembled Porous Protein Materials in Living Cells
2017 StandoutNobel
[Progress in gene therapy].
2011
Engineering Biomolecular Self‐Assembly at Solid–Liquid Interfaces
2020 StandoutNobel
Pre-existing Anti–Adeno-Associated Virus Antibodies as a Challenge in AAV Gene Therapy
2013
Viral Vectors for Gene Therapy: Translational and Clinical Outlook
2015
Targeted Delivery of mRNA with One-Component Ionizable Amphiphilic Janus Dendrimers
2021 StandoutNobel
A Dynamic View of Hepatitis C Virus Replication Complexes
2008 StandoutNobel
Combinatorial Peptide Libraries: Mining for Cell-Binding Peptides
2013
Targeted gene knock-in by homology-directed genome editing using Cas9 ribonucleoprotein and AAV donor delivery
2017 StandoutNobel
Adeno-Associated Virus Type 2 Capsids with Externalized VP1/VP2 Trafficking Domains Are Generated prior to Passage through the Cytoplasm and Are Maintained until Uncoating Occurs in the Nucleus
2006
Disentangling Rotational Dynamics and Ordering Transitions in a System of Self-Organizing Protein Nanorods via Rotationally Invariant Latent Representations
2021 StandoutNobel
Synthetic virology: engineering viruses for gene delivery
2014
Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy
2017
Characterization of the nuclear export adaptor protein Nmd3 in association with the 60S ribosomal subunit
2010 StandoutNobel
Protein Assembly: Versatile Approaches to Construct Highly Ordered Nanostructures
2016
Anomalous diffusion models and their properties: non-stationarity, non-ergodicity, and ageing at the centenary of single particle tracking
2014 Standout
Nontoxic nanopore electroporation for effective intracellular delivery of biological macromolecules
2019 StandoutNobel
Works of Luca Perabò being referenced
Recent developments in adeno‐associated virus vector technology
2008
Adeno-associated virus serotypes 1 to 5 mediated tumor cell directed gene transfer and improvement of transduction efficiency
2005
Optimization of stealth adeno-associated virus vectors by randomization of immunogenic epitopes
2009
In vitro selection of viral vectors with modified tropism: the adeno-associated virus display
2003
Engineering adeno‐associated virus serotype 2‐based targeting vectors using a new insertion site‐position 453‐and single point mutations
2009
Artificial Evolution with Adeno-Associated Viral Libraries
2008
Genetic modifications of the adeno-associated virus type 2 capsid reduce the affinity and the neutralizing effects of human serum antibodies
2003
Receptor targeting of adeno-associated virus vectors
2003
Successful target cell transduction of capsid-engineered rAAV vectors requires clathrin-dependent endocytosis
2011
Combinatorial engineering of a gene therapy vector: directed evolution of adeno‐associated virus
2005
Engineering adeno-associated virus 2 vectors for targeted gene delivery to atherosclerotic lesions
2007
Efficient gene transfer of CD40 ligand into primary B-CLL cells using recombinant adeno-associated virus (rAAV) vectors
2002
Heparan Sulfate Proteoglycan Binding Properties of Adeno-Associated Virus Retargeting Mutants and Consequences for Their In Vivo Tropism
2006
Green Fluorescent Protein-Tagged Adeno-Associated Virus Particles Allow the Study of Cytosolic and Nuclear Trafficking
2005
Gene transfer into human cord blood−derived CD34+ cells by adeno-associated viral vectors
2010
AAV-based gene transfer.
2003