Citation Impact
Citing Papers
Lumacaftor–Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508delCFTR
2015 Standout
Cystic fibrosis
2016 Standout
Human Immune Responses to Adeno-Associated Virus (AAV) Vectors
2020
Cystic fibrosis genetics: from molecular understanding to clinical application
2014 Standout
Safe and Effective In Vivo Targeting and Gene Editing in Hematopoietic Stem Cells: Strategies for Accelerating Development
2021 StandoutNobel
Potentiator ivacaftor abrogates pharmacological correction of ΔF508 CFTR in cystic fibrosis
2014
Works of Kavitha Kotha being referenced
Ivacaftor treatment of cystic fibrosis patients with the G551D mutation: a review of the evidence
2013
Health outcomes in spinal muscular atrophy type 1 following AVXS‐101 gene replacement therapy
2018