Jill A. Morris

Chemically Modified Platforms for Better RNA Therapeutics

Accurate proteome-wide missense variant effect prediction with AlphaMissense

Are we prepared to deliver gene‐targeted therapies for rare diseases?

Niemann-Pick C1 Disease: The I1061T Substitution Is a Frequent Mutant Allele in Patients of Western European Descent and Correlates with a Classic Juvenile Phenotype