Dora Steel

Adeno-associated virus as a delivery vector for gene therapy of human diseases

Polydopamine Nanoparticles Targeting Ferroptosis Mitigate Intervertebral Disc Degeneration Via Reactive Oxygen Species Depletion, Iron Ions Chelation, and GPX4 Ubiquitination Suppression

HOPS-associated neurological disorders (HOPSANDs): linking endolysosomal dysfunction to the pathogenesis of dystonia

AADC deficiency from infancy to adulthood: Symptoms and developmental outcome in an international cohort of 63 patients